Arthur W. Nienhuis

Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B

Amit C. Nathwani, Edward G. D. Tuddenham, Savita Rangarajan et al. · New England Journal of Medicine · 2011 · 1.8K citations · Full text

Medicine, Hematology, Molecular Medicine +13

Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B

Amit Nathwani, Ulreke M. Reiss, Edward G. D. Tuddenham et al. · New England Journal of Medicine · 2014 · 1.3K citations · Full text

Medicine, Genetics, Molecular Genetics +17

Efficacy of Deferoxamine in Preventing Complications of Iron Overload in Patients with Thalassemia Major

Gary M. Brittenham, Patricia Griffith, Arthur W. Nienhuis et al. · New England Journal of Medicine · 1994 · 846 citations · Full text

Medicine, Hematology, Pharmacotherapy +16

5-Azacytidine Selectively Increases γ-Globin Synthesis in a Patient with β⁺Thalassemia

Timothy J. Ley, Joseph DeSimone, Nicholas P. Anagnou et al. · New England Journal of Medicine · 1982 · 496 citations

Medicine, Hematology, Pharmacology +9

Selection of Drug-Resistant Bone Marrow Cells in Vivo After Retroviral Transfer of Human <i>MDR</i> 1

Brian P. Sorrentino, Stephen J. Brandt, David M. Bodine et al. · Science · 1992 · 494 citations

Medicine, Cancer Biology, Pharmacology +14