Roberta Pajno

Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency

Maria Pia Cicalese, Francesca Ferrua, Laura Castagnaro et al. · Blood · 2016 · 217 citations · Full text

Life Sciences, Immunology, Molecular Genetics +14

Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study

Francesca Ferrua, Maria Pia Cicalese, Stefania Galimberti et al. · The Lancet Haematology · 2019 · 208 citations · Full text

Medicine, Hematology, Immunology +15

In vivo tracking of T cells in humans unveils decade-long survival and activity of genetically modified T memory stem cells

Luca Biasco, Serena Scala, Luca Basso‐Ricci et al. · Science Translational Medicine · 2015 · 174 citations

Life Sciences, Cell Biology, Immunology +17

Factors Associated With Severe Gastrointestinal Diagnoses in Children With SARS-CoV-2 Infection or Multisystem Inflammatory Syndrome

Andrea Lo Vecchio, Silvia Garazzino, Andrea Smarrazzo et al. · JAMA Network Open · 2021 · 44 citations · Full text

Medicine, Infectious Diseases, Pediatrics +13

Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency

Maddalena Migliavacca, Federica Barzaghi, Claudia Fossati et al. · Nature Medicine · 2024 · 26 citations · Full text

Medicine, Molecular Biology, Molecular Medicine +16