Maddalena Migliavacca

Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access

Francesca Fumagalli, Valeria Calbi, Maria Grazia Natali Sora et al. · The Lancet · 2022 · 284 citations · Full text

Medicine, Hematology, Immunology +15

Response to Rituximab-Based Therapy and Risk Factor Analysis in Epstein Barr Virus–Related Lymphoproliferative Disorder After Hematopoietic Stem Cell Transplant in Children and Adults: A Study From the Infectious Diseases Working Party of the European Group for Blood and Marrow Transplantation

Jan Styczyński, Lidia Gil, Gloria Tridello et al. · Clinical Infectious Diseases · 2013 · 249 citations · Full text

Medicine, Hematology, Infectious Diseases +13

Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study

Francesca Ferrua, Maria Pia Cicalese, Stefania Galimberti et al. · The Lancet Haematology · 2019 · 208 citations · Full text

Medicine, Hematology, Immunology +15

Interleukin-17–Producing T-Helper Cells as New Potential Player Mediating Graft-Versus-Host Disease in Patients Undergoing Allogeneic Stem-Cell Transplantation

Erica Dander, Adriana Balduzzi, Greta Zappa et al. · Transplantation · 2009 · 129 citations

Life Sciences, Hematology, Immunology +13

Dual-regulated Lentiviral Vector for Gene Therapy of X-linked Chronic Granulomatosis

Maria Serena Chiriacò, Giada Farinelli, Valentina Capo et al. · Molecular Therapy · 2014 · 62 citations · Full text

Life Sciences, Translational Sciences, Cell Therapy +15