Simone Iwabe

Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement

Artur V. Cideciyan, Samuel G. Jacobson, William A. Beltran et al. · Proceedings of the National Academy of Sciences · 2013 · 440 citations · Full text

Medicine, Ophthalmology, Vision Science +17

Gene therapy rescues photoreceptor blindness in dogs and paves the way for treating human X-linked retinitis pigmentosa

William A. Beltran, Artur V. Cideciyan, Alfred S. Lewin et al. · Proceedings of the National Academy of Sciences · 2012 · 260 citations · Full text

Medicine, Ophthalmology, Vision Science +16

Mutation-independent rhodopsin gene therapy by knockdown and replacement with a single AAV vector

Artur V. Cideciyan, Raghavi Sudharsan, Valérie Dufour et al. · Proceedings of the National Academy of Sciences · 2018 · 147 citations · Full text

Medicine, Genetics, Ophthalmology +17

Canine Retina Has a Primate Fovea-Like Bouquet of Cone Photoreceptors Which Is Affected by Inherited Macular Degenerations

William A. Beltran, Artur V. Cideciyan, Karina E Guziewicz et al. · PLoS ONE · 2014 · 130 citations · Full text

Medicine, Neuroscience, Vision Science +17

Successful arrest of photoreceptor and vision loss expands the therapeutic window of retinal gene therapy to later stages of disease

William A. Beltran, Artur V. Cideciyan, Simone Iwabe et al. · Proceedings of the National Academy of Sciences · 2015 · 92 citations · Full text

Medicine, Ophthalmology, Vision Science +17