Michael P. Moazami

Suppression of mutant C9orf72 expression by a potent mixed backbone antisense oligonucleotide

Hélène Tran, Michael P. Moazami, Huiya Yang et al. · Nature Medicine · 2021 · 174 citations · Full text

Life Sciences, Genetics, Molecular Biology +12

Hybrid Aptamer‐Molecularly Imprinted Polymer (aptaMIP) Nanoparticles from Protein Recognition—A Trypsin Model

Mark V. Sullivan, Oliver Clay, Michael P. Moazami et al. · Macromolecular Bioscience · 2021 · 38 citations · Full text

Engineering, Bioengineering, Biotechnology +17

Intratracheally administered LNA gapmer antisense oligonucleotides induce robust gene silencing in mouse lung fibroblasts

Minwook Shin, Io Long Chan, Yuming Cao et al. · Nucleic Acids Research · 2022 · 29 citations · Full text

Life Sciences, Cell Biology, Molecular Biology +16

Locked Nucleic Acid Gapmers and Conjugates Potently Silence ADAM33, an Asthma-Associated Metalloprotease with Nuclear-Localized mRNA

Hannah M. Pendergraff, Pranathi M. Krishnamurthy, Alexandre J. Debacker et al. · Molecular Therapy — Nucleic Acids · 2017 · 27 citations · Full text

Life Sciences, Molecular Biology, Molecular Genetics +15

Quantifying and mitigating motor phenotypes induced by antisense oligonucleotides in the central nervous system

Michael P. Moazami, Julia M Rembetsy-Brown, Samantha L. Sarli et al. · Molecular Therapy · 2024 · 26 citations · Full text

Life Sciences, Molecular Biology, Neuroscience +12