Thibaut Marais

Intravenous Administration of Self-complementary AAV9 Enables Transgene Delivery to Adult Motor Neurons

Sandra Duqué, Béatrice Joussemet, Christel Rivière et al. · Molecular Therapy · 2009 · 488 citations · Full text

Intravenous scAAV9 delivery of a codon-optimized SMN1 sequence rescues SMA mice

Elisa Dominguez, Thibaut Marais, Nicolas Chatauret et al. · Human Molecular Genetics · 2010 · 288 citations · Full text

Intramuscular scAAV9-SMN Injection Mediates Widespread Gene Delivery to the Spinal Cord and Decreases Disease Severity in SMA Mice

Sofia Benkhelifa‐Ziyyat, Aurore Besse, Marianne Roda et al. · Molecular Therapy · 2013 · 127 citations · Full text

Systemic AAVrh10 provides higher transgene expression than AAV9 in the brain and the spinal cord of neonatal mice

Yannick Tanguy, Maria Grazia Biferi, Aurore Besse et al. · Frontiers in Molecular Neuroscience · 2015 · 96 citations · Full text

Systemic Aavrh10, Immunology, Transduction Efficiency +16

The autophagy/lysosome pathway is impaired in SCA7 patients and SCA7 knock-in mice

Sandro Alves, Florence Cormier‐Dequaire, Martina Marinello et al. · Acta Neuropathologica · 2014 · 69 citations

Knockout Mouse, Cell Autophagy, Mitophagy +13