Sofia Benkhelifa‐Ziyyat

Intravenous scAAV9 delivery of a codon-optimized SMN1 sequence rescues SMA mice

Elisa Dominguez, Thibaut Marais, Nicolas Chatauret et al. · Human Molecular Genetics · 2010 · 288 citations · Full text

Intramuscular scAAV9-SMN Injection Mediates Widespread Gene Delivery to the Spinal Cord and Decreases Disease Severity in SMA Mice

Sofia Benkhelifa‐Ziyyat, Aurore Besse, Marianne Roda et al. · Molecular Therapy · 2013 · 127 citations · Full text

Quantification of lentiviral vector copy numbers in individual hematopoietic colony-forming cells shows vector dose-dependent effects on the frequency and level of transduction

Sabine Charrier, Marina Ferrand, Madeleine Zerbato et al. · Gene Therapy · 2010 · 104 citations · Full text

Phosphorylation of MafA Is Essential for Its Transcriptional and Biological Properties

Sofia Benkhelifa‐Ziyyat, Sylvain Provot, Eugène Nabais et al. · Molecular and Cellular Biology · 2001 · 91 citations · Full text

Biological Properties, Mafa Is Essential, Transcriptional Regulation +20

Interaction of Maf Transcription Factors with Pax-6 Results in Synergistic Activation of the Glucagon Promoter

Nathalie Planque, Laurence Leconte, Frédéric M. Coquelle et al. · Journal of Biological Chemistry · 2001 · 81 citations · Full text