Rebecca Holley

Neuropathology in Mouse Models of Mucopolysaccharidosis Type I, IIIA and IIIB

Fiona L. Wilkinson, Rebecca Holley, Kia Langford‐Smith et al. · PLoS ONE · 2012 · 189 citations · Full text

Life Sciences, Neurology, Neuroscience +17

Mapping the Differential Distribution of Glycosaminoglycans in the Adult Human Retina, Choroid, and Sclera

Simon J. Clark, Tiarnán D L Keenan, Helen L. Fielder et al. · Investigative Ophthalmology & Visual Science · 2011 · 131 citations · Full text

Life Sciences, Biochemistry, Ophthalmology +14

A novel adeno-associated virus capsid with enhanced neurotropism corrects a lysosomal transmembrane enzyme deficiency

Julie Tordo, Claire O’Leary, André Saraiva Leão Marcelo Antunes et al. · Brain · 2018 · 127 citations · Full text

Life Sciences, Biotechnology, Molecular Biology +15

Hematopoietic Stem Cell and Gene Therapy Corrects Primary Neuropathology and Behavior in Mucopolysaccharidosis IIIA Mice

Alex Langford-Smith, Fiona L. Wilkinson, Kia Langford‐Smith et al. · Molecular Therapy · 2012 · 96 citations · Full text

Medicine, Neurology, Neuroscience +17

Brain‐targeted stem cell gene therapy corrects mucopolysaccharidosis type II via multiple mechanisms

Hélène F.E. Gleitz, Ai Yin Liao, James Cook et al. · EMBO Molecular Medicine · 2018 · 87 citations · Full text

Medicine, Neurology, Neuroscience +17