Three-Dimensional Human iPSC-Derived Artificial Skeletal Muscles Model Muscular Dystrophies and Enable Multilineage Tissue Engineering

Sara M. Maffioletti, Shilpita Sarcar, A. Henderson, +19

Cell Reports

Explant culture: a simple, reproducible, efficient and economic technique for isolation of mesenchymal stromal cells from human adipose tissue and lipoaspirate

Nancy Priya, Shilpita Sarcar, Anish Sen Majumdar, +1

Journal of Tissue Engineering and Regenerative Medicine

Computationally designed liver-specific transcriptional modules and hyperactive factor IX improve hepatic gene therapy

Nisha Nair, Melvin Y. Rincón, Hanneke Evens, +9

Blood

Efficient In Vivo Liver-Directed Gene Editing Using CRISPR/Cas9

Kshitiz Singh, Hanneke Evens, Nisha Nair, +5

Molecular Therapy

Modeling Skeletal Muscle Laminopathies Using Human Induced Pluripotent Stem Cells Carrying Pathogenic LMNA Mutations

Heather B. Steele-Stallard, Luca Pinton, Shilpita Sarcar, +4

Frontiers in Physiology

Next-generation muscle-directed gene therapy by in silico vector design

Shilpita Sarcar, Warut Tulalamba, Melvin Y. Rincón, +16

Nature Communications

Genome-wide Computational Analysis Reveals Cardiomyocyte-specific Transcriptional Cis-regulatory Motifs That Enable Efficient Cardiac Gene Therapy

Melvin Y. Rincón, Shilpita Sarcar, Dina Danso‐Abeam, +10

Molecular Therapy