Kshitiz Singh

In utero CRISPR-mediated therapeutic editing of metabolic genes

Avery C. Rossidis, John D. Stratigis, Alexandra C. Chadwick et al. · Nature Medicine · 2018 · 213 citations · Full text

Engineering, Genome Surgery, Medicine +8

In utero gene editing for monogenic lung disease

Deepthi Alapati, William J. Zacharias, Heather A. Hartman et al. · Science Translational Medicine · 2019 · 113 citations · Full text

Efficient CRISPR/Cas9-mediated editing of trinucleotide repeat expansion in myotonic dystrophy patient-derived iPS and myogenic cells

Sumitava Dastidar, Simon Ardui, Kshitiz Singh et al. · Nucleic Acids Research · 2018 · 92 citations · Full text

Efficient In Vivo Liver-Directed Gene Editing Using CRISPR/Cas9

Kshitiz Singh, Hanneke Evens, Nisha Nair et al. · Molecular Therapy · 2018 · 63 citations · Full text

In utero adenine base editing corrects multi-organ pathology in a lethal lysosomal storage disease

Sourav K. Bose, Brandon M. White, Meghana V. Kashyap et al. · Nature Communications · 2021 · 61 citations · Full text

Genetics, Utero Base Editing, Pathology +18