Julie Brault

Enhanced homology-directed repair for highly efficient gene editing in hematopoietic stem/progenitor cells

Suk See De Ravin, Julie Brault, Ronald J. Meis et al. · Blood · 2021 · 74 citations · Full text

Life Sciences, Genetics, Molecular Biology +14

Correction of X-CGD patient HSPCs by targeted CYBB cDNA insertion using CRISPR/Cas9 with 53BP1 inhibition for enhanced homology-directed repair

Colin L. Sweeney, Mara Pavel-Dinu, Uimook Choi et al. · Gene Therapy · 2021 · 52 citations · Full text

Life Sciences, Genetics, Molecular Biology +16

Lentivector cryptic splicing mediates increase in CD34+ clones expressing truncated HMGA2 in human X-linked severe combined immunodeficiency

Suk See De Ravin, Siyuan Liu, Colin L. Sweeney et al. · Nature Communications · 2022 · 48 citations · Full text

Life Sciences, Hematology, Immunology +17

CRISPR-targeted<i>MAGT1</i>insertion restores XMEN patient hematopoietic stem cells and lymphocytes

Julie Brault, Taylor Liu, Ezekiel Bello et al. · Blood · 2021 · 37 citations · Full text

Life Sciences, Genetics, Molecular Genetics +12

Optimized Generation of Functional Neutrophils and Macrophages from Patient-Specific Induced Pluripotent Stem Cells: <i>Ex Vivo</i> Models of X ⁰ -Linked, AR22 ⁰ - and AR47 ⁰ - Chronic Granulomatous Diseases

Julie Brault, Erwan Goutagny, Narasimha Swamy Telugu et al. · BioResearch open access · 2014 · 33 citations · Full text

Life Sciences, Cell Biology, Molecular Genetics +17