Anna Mollin

PTC124 targets genetic disorders caused by nonsense mutations

Ellen Welch, Elisabeth R. Barton, Jin Zhuo et al. · Nature · 2007 · 1.1K citations

Life Sciences, Genetics, Molecular Genetics +8

Structure–Activity Relationship (SAR) Optimization of 6-(Indol-2-yl)pyridine-3-sulfonamides: Identification of Potent, Selective, and Orally Bioavailable Small Molecules Targeting Hepatitis C (HCV) NS4B

Nanjing Zhang, Xiaoyan Zhang, Jin Zhu et al. · Journal of Medicinal Chemistry · 2013 · 43 citations · Full text

Pharmacy, Medicinal Chemistry, Pharmacology +17

The minor gentamicin complex component, X2, is a potent premature stop codon readthrough molecule with therapeutic potential

Westley J. Friesen, Briana Johnson, Jairo Sierra et al. · PLoS ONE · 2018 · 38 citations · Full text

Medicine, Pharmacology, Pharmacotherapy +14

Pharmacokinetics, pharmacodynamics, and efficacy of a small-molecule<i>SMN2</i>splicing modifier in mouse models of spinal muscular atrophy

Xin Zhao, Zhihua Feng, Karen Ling et al. · Human Molecular Genetics · 2016 · 35 citations · Full text

Life Sciences, Molecular Biology, Pharmacology +17

Effective Delivery of a Microtubule Polymerization Inhibitor Synergizes with Standard Regimens in Models of Pancreatic Ductal Adenocarcinoma

Jaime Eberle-Singh, Irina R. Sagalovskiy, H. Carlo Maurer et al. · Clinical Cancer Research · 2019 · 35 citations

Medicine, Oncology, Pharmacology +16