Georgia R. Lill

Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells

Megan D. Hoban, Gregory J. Cost, Matthew Mendel et al. · Blood · 2015 · 318 citations · Full text

CRISPR/Cas9-Mediated Correction of the Sickle Mutation in Human CD34+ cells

Megan D. Hoban, Dianne Lumaquin, Caroline Y. Kuo et al. · Molecular Therapy · 2016 · 213 citations · Full text

Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome

Caroline Y. Kuo, Joseph Long, Beatriz Campo-Fernández et al. · Cell Reports · 2018 · 137 citations · Full text

Reactivating Fetal Hemoglobin Expression in Human Adult Erythroblasts Through BCL11A Knockdown Using Targeted Endonucleases

Michelle Mojadidi, John W. Phillips, Caroline Y. Kuo et al. · Molecular Therapy — Nucleic Acids · 2016 · 56 citations · Full text

Cytoreductive conditioning intensity predicts clonal diversity in ADA-SCID retroviral gene therapy patients

Aaron Cooper, Georgia R. Lill, Kit L. Shaw et al. · Blood · 2017 · 30 citations · Full text