Concepedia
3
Publications
164
Citations
H-Index
2019
Active since
Affiliations
UniQure (Netherlands)(Current)
Leiden University Medical Center
Elisabeth A Spronck is an author at UniQure (Netherlands).
Publications per year
2019–2021
AAV5-miHTT Gene Therapy Demonstrates Sustained Huntingtin Lowering and Functional Improvement in Huntington Disease Mouse Models
Elisabeth A Spronck, Cynthia Brouwers, Astrid Vallès et al. · Molecular Therapy — Methods & Clinical Development · 2019 · 85 citations · Full text
Intrastriatal Administration of AAV5-miHTT in Non-Human Primates and Rats Is Well Tolerated and Results in miHTT Transgene Expression in Key Areas of Huntington Disease Pathology
Elisabeth A Spronck, Astrid Vallès, Margit H. Lampen et al. · Brain Sciences · 2021 · 46 citations · Full text
Enhanced Factor IX Activity following Administration of AAV5-R338L “Padua” Factor IX versus AAV5 WT Human Factor IX in NHPs
Elisabeth A Spronck, Ying Poi Liu, Jacek Lubelski et al. · Molecular Therapy — Methods & Clinical Development · 2019 · 33 citations · Full text
Rows per page
1–3 of 3