Leillani L. Ha

Custom CRISPR–Cas9 PAM variants via scalable engineering and machine learning

Rachel A. Silverstein, Nahye Kim, Ann-Sophie Kroell et al. · Nature · 2025 · 61 citations · Full text

Life Sciences, Biotechnology, Genetics +13

In situ architecture of Opa1-dependent mitochondrial cristae remodeling

Michelle Y. Fry, Paula P. Navarro, Pusparanee Hakim et al. · The EMBO Journal · 2024 · 57 citations · Full text

Life Sciences, Biochemistry, Cell Biology +17

Optimization of base editors for the functional correction of SMN2 as a treatment for spinal muscular atrophy

Christiano R. R. Alves, Leillani L. Ha, Rebecca Yaworski et al. · Nature Biomedical Engineering · 2023 · 42 citations · Full text

Medicine, Neurology, Neuroscience +3

Base editing as a genetic treatment for spinal muscular atrophy

Christiano R. R. Alves, Leillani L. Ha, Rebecca Yaworski et al. · bioRxiv (Cold Spring Harbor Laboratory) · 2023 · 19 citations · Full text

Life Sciences, Genetics, Molecular Genetics +17

<i>In situ</i> architecture of Opa1-dependent mitochondrial cristae remodeling

Michelle Y. Fry, Paula P. Navarro, Pusparanee Hakim et al. · bioRxiv (Cold Spring Harbor Laboratory) · 2023 · 11 citations · Full text

Life Sciences, Biochemistry, Cell Biology +17