David A. Shivak

Translating dosage compensation to trisomy 21

Jun Jiang, Yuanchun Jing, Gregory J. Cost et al. · Nature · 2013 · 342 citations · Full text

Medicine, Translational Sciences, Cytogenetics +5

In vivo genome editing of the albumin locus as a platform for protein replacement therapy

Rajiv P. Sharma, Xavier M. Anguela, Yannick Doyon et al. · Blood · 2015 · 298 citations · Full text

Life Sciences, Genetics, Molecular Biology +16

Homology-driven genome editing in hematopoietic stem and progenitor cells using ZFN mRNA and AAV6 donors

Jianbin Wang, Colin M. Exline, Joshua J. DeClercq et al. · Nature Biotechnology · 2015 · 264 citations

Life Sciences, Molecular Biology, Molecular Genetics +15

Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington’s disease

Bryan Zeitler, Steven Froelich, Kimberly Marlen et al. · Nature Medicine · 2019 · 220 citations

Life Sciences, Genetics, Molecular Biology +16

Targeted gene addition in human CD34+ hematopoietic cells for correction of X-linked chronic granulomatous disease

Suk See De Ravin, Andreas Reik, Peiqi Liu et al. · Nature Biotechnology · 2016 · 193 citations · Full text

Medicine, Hematology, Molecular Genetics +12