Klaus Kühlcke

Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1

Marion Ott, Manfred Schmidt, Kerstin Schwarzwaelder et al. · Nature Medicine · 2006 · 1.2K citations

Gene Therapies, Autoimmune Disease, Novel Therapy +10

Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease

Stefan Stein, Marion Ott, Stephan Schultze‐Strasser et al. · Nature Medicine · 2010 · 774 citations · Full text

Hematological Malignancy, Autoimmune Disease, Granulocyte +12

Murine Leukemia Induced by Retroviral Gene Marking

Zhixiong Li, J. Düllmann, Bernd Schiedlmeier et al. · Science · 2002 · 654 citations

Mixed-phenotype Acute Leukemia, Genetics, Immunology +18

Gene Therapy for Wiskott-Aldrich Syndrome—Long-Term Efficacy and Genotoxicity

Christian Braun, Kaan Boztuǧ, Anna Paruzynski et al. · Science Translational Medicine · 2014 · 543 citations · Full text

Stem-Cell Gene Therapy for the Wiskott–Aldrich Syndrome

Kaan Boztuǧ, Manfred Schmidt, Adrian Schwarzer et al. · New England Journal of Medicine · 2010 · 532 citations · Full text

Cell Therapy, Immunology, Blood Cell +24