Chantal Brouzes

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

Alexis A. Thompson, Mark C. Walters, Janet L. Kwiatkowski et al. · New England Journal of Medicine · 2018 · 646 citations · Full text

Type I interferon-mediated autoinflammation due to DNase II deficiency

Mathieu P. Rodero, Alessandra Tesser, Eva Bartok et al. · Nature Communications · 2017 · 217 citations · Full text

Long-term outcomes of lentiviral gene therapy for the β-hemoglobinopathies: the HGB-205 trial

Elisa Magrin, Michaëla Semeraro, Nicolas Hebert et al. · Nature Medicine · 2022 · 99 citations

Gene Therapies, Lentiviral Gene Therapy, Immunodeficiencies +9

X-linked primary immunodeficiency associated with hemizygous mutations in the moesin (MSN) gene

Chantal Lagresle‐Peyrou, Sonia Luce, Farid Ouchani et al. · Journal of Allergy and Clinical Immunology · 2016 · 87 citations · Full text

Primary Immunodeficiency, X-linked Primary Immunodeficiency, Autoimmune Disease +10

Sotatercept, a novel transforming growth factor β ligand trap, improves anemia in β-thalassemia: a phase II, open-label, dose-finding study

Maria Domenica Cappellini, John B. Porter, Raffaella Origa et al. · Haematologica · 2018 · 85 citations · Full text

Dose-finding Study, Immunohematology, Human Growth +18