Elisa Magrin

Gene Therapy in a Patient with Sickle Cell Disease

Jean‐Antoine Ribeil, Salima Hacein‐Bey‐Abina, Emmanuel Payen et al. · New England Journal of Medicine · 2017 · 669 citations · Full text

Medicine, Genetics, Hematology +17

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

Alexis A. Thompson, Mark C. Walters, Janet L. Kwiatkowski et al. · New England Journal of Medicine · 2018 · 661 citations · Full text

Medicine, Genetics, Hematology +16

Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human β-globin locus

Chiara Antoniani, Vasco Meneghini, Annalisa Lattanzi et al. · Blood · 2018 · 187 citations · Full text

Life Sciences, Genetics, Molecular Genetics +15

Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott–Aldrich syndrome

Alessandra Magnani, Michaëla Semeraro, Frédéric Adam et al. · Nature Medicine · 2022 · 118 citations · Full text

Medicine, Hematology, Immunology +17

Plerixafor enables safe, rapid, efficient mobilization of hematopoietic stem cells in sickle cell disease patients after exchange transfusion

Chantal Lagresle‐Peyrou, François Lefrère, Elisa Magrin et al. · Haematologica · 2018 · 110 citations · Full text

Medicine, Cell Biology, Hematology +17