François Lefrère

Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy

Nathalie Cartier, Salima Hacein‐Bey‐Abina, Cynthia C. Bartholomae et al. · Science · 2009 · 1.5K citations · Full text

Medicine, Neurology, Neuroscience +17

Efficacy of romiplostim in patients with chronic immune thrombocytopenic purpura: a double-blind randomised controlled trial

David J. Kuter, James B. Bussel, Roger M. Lyons et al. · The Lancet · 2008 · 862 citations

Medicine, Hematology, Pharmacology +6

Regression of Splenic Lymphoma with Villous Lymphocytes after Treatment of Hepatitis C Virus Infection

Olivier Hermine, François Lefrère, Jean–Pierre Bronowicki et al. · New England Journal of Medicine · 2002 · 799 citations · Full text

Medicine, Hematology, Pathology +16

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

Alexis A. Thompson, Mark C. Walters, Janet L. Kwiatkowski et al. · New England Journal of Medicine · 2018 · 661 citations · Full text

Medicine, Genetics, Hematology +16

Outcomes Following Gene Therapy in Patients With Severe Wiskott-Aldrich Syndrome

Salima Hacein-Bey Abina, H. Bobby Gaspar, Johanna Blondeau et al. · JAMA · 2015 · 379 citations · Full text

Medicine, Hematology, Immunology +17