Gabriella Allegri

Treatment of a metabolic liver disease by in vivo genome base editing in adult mice

Lukas Villiger, Hiu Man Grisch‐Chan, Helen Lindsay et al. · Nature Medicine · 2018 · 440 citations

Life Sciences, Genetics, Molecular Genetics +15

Lipid nanoparticle-targeted mRNA therapy as a treatment for the inherited metabolic liver disorder arginase deficiency

Brian Truong, Gabriella Allegri, Xiaobo Liu et al. · Proceedings of the National Academy of Sciences · 2019 · 154 citations · Full text

Life Sciences, Biochemistry, Molecular Biology +17

Enhancement of hepatic autophagy increases ureagenesis and protects against hyperammonemia

Leandro R. Soria, Gabriella Allegri, Dominique Melck et al. · Proceedings of the National Academy of Sciences · 2017 · 57 citations · Full text

Life Sciences, Biochemistry, Cell Biology +17

Brain catecholamine depletion and motor impairment in a<i>Th</i>knock-in mouse with type B tyrosine hydroxylase deficiency

Germaine Korner, Daniela Noaín, Ming Ying et al. · Brain · 2015 · 36 citations · Full text

Life Sciences, Genetics, Neuroscience +17

Glycogen storage disease type VI: clinical course and molecular background

Tim Aeppli, Daisy Rymen, Gabriella Allegri et al. · European Journal of Pediatrics · 2019 · 30 citations

Life Sciences, Genetics, Molecular Biology +12