Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors

M. H. Tan, A. J. Smith, B. Pawlyk, X. Xu, X. Liu, James Bainbridge, M. Basche, J. McIntosh, H. V. Tran, A. Nathwani,

Human Molecular Genetics · 2009 · 15 citations · 0 references

DOIFull text

Open access

Concepts

Abstract

Human Molecular Genetics 2009 18:12; pp. 2099–2114; doi:10.1093/hmg/ddp133 The Authors regret that there was an error in the Copyright status of paper ‘10.1093/hmg/ddp133’. The article is now freely available online under the Oxford Open model and the copyright line should have read: © The Author 2009. Published by Oxford University Press. This is an Open Access article distributed under the terms of the Creative Commons Attribution Non-Commercial License (http://creativecommons.org/licenses/by-nc/2.5), which permits unrestricted non-commercial use, distribution, and reproduction in any medium, provided the original work is properly cited.