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Rescue of a lysosomal storage disorder caused by Grn loss of function with a brain penetrant progranulin biologic

Neurodegenerative DiseasesMolecular NeuroscienceLysosomal Storage DisorderNeurological DisorderDegenerative DiseaseGrn LossPrion DiseaseNeuroscienceNeurologyBrain PathologyNeuropathologyMedicineLysosomal Storage DiseaseSocial Sciences