Concepedia

A long-term study of AAV gene therapy in dogs with hemophilia A identifies clonal expansions of transduced liver cells

Giang N. Nguyen, J.K. Everett, Samita Kafle, Aoife M. Roche, Hayley E. Raymond, Jacob S. Leiby, Christian M. Wood, Charles‐Antoine Assenmacher, Elizabeth P. Merricks, Christian Long,

Nature Biotechnology · 2020 · 445 citations · 47 references

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47

<tt>BLAT</tt>—The <tt>BLAST</tt>-Like Alignment Tool

W. James Kent · Genome Research · 2002 · 8.4K citations · Full text

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NCBI reference sequences (RefSeq): a curated non-redundant sequence database of genomes, transcripts and proteins

Kim D. Pruitt, Tatiana Tatusova, D. R. Maglott · Nucleic Acids Research · 2006 · 4.7K citations · Full text

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NCBI Reference Sequence (RefSeq): a curated non-redundant sequence database of genomes, transcripts and proteins

Kim D. Pruitt · Nucleic Acids Research · 2004 · 1.7K citations · Full text

, , +17

Implementing a Class of Permutation Tests: The<b>coin</b>Package

Torsten Hothorn, Kurt Hornik, Mark A. van de Wiel et al. · Journal of Statistical Software · 2008 · 1.5K citations · Full text

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Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B

Amit Nathwani, Ulreke M. Reiss, Edward G. D. Tuddenham et al. · New England Journal of Medicine · 2014 · 1.3K citations · Full text

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