In vitro assay for the efficacy assessment of AAV vectors expressing microdystrophin

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X chromosome-linked muscular dystrophy (mdx) in the mouse.

G. Bulfield, W. G. Siller, P.A.L. Wight et al. · Proceedings of the National Academy of Sciences · 1984 · 1.8K citations · Full text

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The Molecular Basis of Muscular Dystrophy in the <i>mdx</i> Mouse: a Point Mutation

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