Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR - Concepedia

Concepedia

Publication | Open Access

Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR

DOI Full Paper Access

343

Citations

22

References

2020

Year

Jasmina Cehajic‐Kapetanovic, Kanmin Xue, Cristina Martínez-Fernández de la Cámara, Anika Nanda, Alexandra Davies, Laura J. Taylor, Anna Paola Salvetti, M. Dominik Fischer, James Aylward, Alun R. Barnard,

Nature Medicine

Initial ResultsEngineeringSomatic VariantGenetic DisorderMedicineGeneticsNovel TherapyMendelian DisorderPathologyGenetic EngineeringDisease Gene IdentificationX-linked Retinitis PigmentosaMolecular DiagnosticsGenome Editing

References

	Year	Citations

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