Concepedia

Non-immunogenic utrophin gene therapy for the treatment of muscular dystrophy animal models

Yafeng Song, Leon Morales, Alock Malik, Andrew Frederick Mead, Christopher Greer, Marilyn A. Mitchell, Mihail T. Petrov, Leonard T. Su, Margaret E. Choi, Shira T. Rosenblum,

Nature Medicine · 2019 · 91 citations · 46 references

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46

Basic local alignment search tool

Stephen F. Altschul, Warren Gish, Webb Miller et al. · Journal of Molecular Biology · 1990 · 94.5K citations

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Dystrophin: The protein product of the duchenne muscular dystrophy locus

Eric P. Hoffman, Robert H. Brown, Louis M. Kunkel · Cell · 1987 · 4.7K citations

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The complete sequence of dystrophin predicts a rod-shaped cytoskeletal protein

Anthony P. Monaco, Louis M. Kunkel · Cell · 1988 · 1.5K citations

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Dystrophin protects the sarcolemma from stresses developed during muscle contraction.

Basil J. Petrof, Joseph B. Shrager, Hansell H. Stedman et al. · Proceedings of the National Academy of Sciences · 1993 · 1.5K citations

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Analysis of AAV Serotypes 1–9 Mediated Gene Expression and Tropism in Mice After Systemic Injection

Carmela Zincarelli, Stephen Soltys, Giuseppe Rengo et al. · Molecular Therapy · 2008 · 1.5K citations · Full text

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