Publication | Open Access

Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction

Genetic DiseasesIn Vivo Gene TherapyNatural SciencesGeneticsGenetic EngineeringMolecular BiologyIntron-targeting Gene IntegrationMolecular GeneticsGenome EngineeringGene EditingMedicineGenome EditingGenetic Disease CorrectionGene Transfer