Efficacy of low dose nitisinone in the management of alkaptonuria

Natural History of Alkaptonuria

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A 3-year randomized therapeutic trial of nitisinone in alkaptonuria

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Use of nitisinone in patients with alkaptonuria

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Medicine, Internal Medicine, Pharmacotherapy +2

Suitability Of Nitisinone In Alkaptonuria 1 (SONIA 1): an international, multicentre, randomised, open-label, no-treatment controlled, parallel-group, dose-response study to investigate the effect of once daily nitisinone on 24-h urinary homogentisic acid excretion in patients with alkaptonuria after 4 weeks of treatment

L. Ranganath, Anna M. Milan, Andrew T. Hughes et al. · Annals of the Rheumatic Diseases · 2014 · 157 citations · Full text

Medicine, Pharmacology, Pharmacotherapy +6