Concepedia

Publication | Open Access

Nusinersen in later-onset spinal muscular atrophy

DOIFull Paper Access

256

Citations

23

References

2019

Year

Basil T. Darras, Claudia A. Chiriboga, Susan T. Iannaccone, Kathryn J. Swoboda, Jacqueline Montes, Laurence Mignon, Shuting Xia, C. Frank Bennett, Kathie M. Bishop, Jeremy M. Shefner,
Neurology

Abstract

This study provides Class IV evidence that nusinersen improves motor function in children with later-onset SMA.

References

YearCitations

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