Efficacy of systemic sirolimus in the treatment of generalized lymphatic anomaly and Gorham–Stout disease - Concepedia

Concepedia

Publication | Open Access

Efficacy of systemic sirolimus in the treatment of generalized lymphatic anomaly and Gorham–Stout disease

DOI Full Paper Access

114

Citations

18

References

2019

Year

Kiersten Ricci, Adrienne M. Hammill, Paula S. Mobberley‐Schuman, Stephen C. Nelson, Julie Blatt, Julia Glade Bender, Catherine McCuaïg, Anna Synakiewicz, Ilona J. Frieden, Denise M. Adams

Pediatric Blood & Cancer

Abstract

Sirolimus appears effective at stabilizing or reducing signs/symptoms of disease in patients with GLA and GSD. Functional impairment and/or QOL improved in the majority of individuals with GLA and GSD with sirolimus treatment.

References

	Year	Citations

Page 1