Longitudinal In Vivo Monitoring of the CNS Demonstrates the Efficacy of Gene Therapy in a Sheep Model of CLN5 Batten Disease - Concepedia

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Publication | Open Access

Longitudinal In Vivo Monitoring of the CNS Demonstrates the Efficacy of Gene Therapy in a Sheep Model of CLN5 Batten Disease

DOI Full Paper Access

94

Citations

37

References

2018

Year

Nadia L. Mitchell, Katharina N. Russell, Martin Wellby, Hollie E. Wicky, Lucia Schoderboeck, Graham K. Barrell, Tracy R. Melzer, Steven J. Gray, Stephanie M. Hughes, David N. Palmer

Molecular Therapy

Knockout MouseEngineeringIn Vivo Gene TherapyMedicineGeneticsGenetic EngineeringAnimal ModelsVivo MonitoringCln5 Batten DiseaseDisease Gene IdentificationMolecular DiagnosticsCell BiologyGenome EditingAnimal GeneticsGene Transfer

References

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