Concepedia

Longitudinal In Vivo Monitoring of the CNS Demonstrates the Efficacy of Gene Therapy in a Sheep Model of CLN5 Batten Disease

Nadia L. Mitchell, Katharina N. Russell, Martin Wellby, Hollie E. Wicky, Lucia Schoderboeck, Graham K. Barrell, Tracy R. Melzer, Steven J. Gray, Stephanie M. Hughes, David N. Palmer

Molecular Therapy · 2018 · 94 citations · 37 references

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37

3D Slicer as an image computing platform for the Quantitative Imaging Network

Andriy Fedorov, Reinhard Beichel, Jayashree Kalpathy–Cramer et al. · Magnetic Resonance Imaging · 2012 · 8.9K citations · Full text

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Self-complementary recombinant adeno-associated virus (scAAV) vectors promote efficient transduction independently of DNA synthesis

DM McCarty, PE Monahan, RJ Samulski · Gene Therapy · 2001 · 725 citations

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The sheep genome illuminates biology of the rumen and lipid metabolism

Yu Jiang, Min Xie, Wenbin Chen et al. · Science · 2014 · 558 citations · Full text

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Preclinical Differences of Intravascular AAV9 Delivery to Neurons and Glia: A Comparative Study of Adult Mice and Nonhuman Primates

Steven J. Gray, Valérie Matagne, Lavanya Bachaboina et al. · Molecular Therapy · 2011 · 504 citations · Full text

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Optimizing Promoters for Recombinant Adeno-Associated Virus-Mediated Gene Expression in the Peripheral and Central Nervous System Using Self-Complementary Vectors

Steven J. Gray, Stacey Beth Foti, Joel Schwartz et al. · Human Gene Therapy · 2011 · 417 citations

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