Efficacy and safety of ataluren in patients with nonsense-mutation cystic fibrosis not receiving chronic inhaled aminoglycosides: The international, randomized, double-blind, placebo-controlled Ataluren Confirmatory Trial in Cystic Fibrosis (ACT CF)

Publication | Open Access

DOI Full Paper Access

Citations

References

2020

Year

Michael W. Konstan, Donald R. VanDevanter, Steven M. Rowe, M. Wilschanski, Eitan Kerem, Isabelle Sermet‐Gaudelus, Emily DiMango, Paola Melotti, Joseph McIntosh, K. De Boeck

Journal of Cystic Fibrosis

Pulmonary CareAct CfClinical TrialsNonsense-mutation Cystic FibrosisMedicinePulmonary Disease