Concepedia

Efficacy and safety of ataluren in patients with nonsense-mutation cystic fibrosis not receiving chronic inhaled aminoglycosides: The international, randomized, double-blind, placebo-controlled Ataluren Confirmatory Trial in Cystic Fibrosis (ACT CF)

Michael W. Konstan, Donald R. VanDevanter, Steven M. Rowe, M. Wilschanski, Eitan Kerem, Isabelle Sermet‐Gaudelus, Emily DiMango, Paola Melotti, Joseph McIntosh, K. De Boeck

Journal of Cystic Fibrosis · 2020 · 65 citations · 23 references

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References

23

Standardisation of spirometry

Martin R. Miller, J. Hankinson, Vito Brusasco et al. · European Respiratory Journal · 2005 · 15.7K citations · Full text

, , +17

Spirometric Reference Values from a Sample of the General U.S. Population

John Hankinson, John Odencrantz, Kathleen B. Fedan · American Journal of Respiratory and Critical Care Medicine · 1999 · 4.3K citations

, , +16

Effect of Aerosolized Recombinant Human DNase on Exacerbations of Respiratory Symptoms and on Pulmonary Function in Patients with Cystic Fibrosis

Henry J. Fuchs, Drucy Borowitz, David Høyrup Christiansen et al. · New England Journal of Medicine · 1994 · 1.5K citations · Full text

, , +14

PTC124 targets genetic disorders caused by nonsense mutations

Ellen Welch, Elisabeth R. Barton, Jin Zhuo et al. · Nature · 2007 · 1.1K citations

, , +8

Correlation between Genotype and Phenotype in Patients with Cystic Fibrosis

New England Journal of Medicine · 1993 · 564 citations · Full text

, , +10