Concepedia

Publication | Open Access

Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction

DOIFull Paper Access

75

Citations

36

References

2017

Year

Sang-oh Han, Giuseppe Ronzitti, Benjamin Arnson, Christian Leborgne, Songtao Li, Federico Mingozzi, Dwight D. Koeberl
Molecular Therapy — Methods & Clinical Development

References

YearCitations

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