Leszek Lisowski

Selection and evaluation of clinically relevant AAV variants in a xenograft liver model

Leszek Lisowski, Allison Dane, Kirk Chu et al. · Nature · 2013 · 452 citations

Life Sciences, Genetics, Molecular Medicine +11

Human <i>COL7A1</i> -corrected induced pluripotent stem cells for the treatment of recessive dystrophic epidermolysis bullosa

Vittorio Sebastiano, Hanson H. Zhen, Bahareh Haddad et al. · Science Translational Medicine · 2014 · 214 citations

Medicine, Biotechnology, Dermatology +14

Genome Editing of Isogenic Human Induced Pluripotent Stem Cells Recapitulates Long QT Phenotype for Drug Testing

Yongming Wang, Ping Liang, Feng Lan et al. · Journal of the American College of Cardiology · 2014 · 174 citations

Life Sciences, Genetics, Molecular Genetics +13

The Balance of Stromal BMP Signaling Mediated by GREM1 and ISLR Drives Colorectal Carcinogenesis

Hiroki Kobayashi, Krystyna A. Gieniec, Josephine A. Wright et al. · Gastroenterology · 2020 · 167 citations · Full text

Medicine, Cancer Biology, Molecular Biology +14

Bioengineered AAV Capsids with Combined High Human Liver Transduction In Vivo and Unique Humoral Seroreactivity

Nicole K. Paulk, Katja Pekrun, Erhua Zhu et al. · Molecular Therapy · 2017 · 164 citations · Full text

Life Sciences, Biomolecular Engineering, Molecular Biology +11