Publication | Open Access
A genome-editing strategy to treat β-hemoglobinopathies that recapitulates a mutation associated with a benign genetic condition
376
Citations
15
References
2016
Year
Benign Genetic ConditionGenetic DisorderMedicineGeneticsGenome-editing StrategyHematologyNatural SciencesMolecular BiologyGenome EngineeringDisease Gene IdentificationMolecular DiagnosticsGenome Editing
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