Neurocognition across the spectrum of mucopolysaccharidosis type I: Age, severity, and treatment

Elsa Shapiro, Igor Nestrašil, Kyle Rudser, Kathleen Delaney, Victor Kovac, Alia Ahmed, Brianna Yund, Paul J. Orchard, Julie B. Eisengart, Gregory R. Niklason,

Molecular Genetics and Metabolism · 2015 · 68 citations · 31 references

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