Long-distance axonal regeneration induced by CNTF gene transfer is impaired by axonal misguidance in the injured adult optic nerve

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Effect of Gene Therapy on Visual Function in Leber's Congenital Amaurosis

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Promoting Axon Regeneration in the Adult CNS by Modulation of the PTEN/mTOR Pathway

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Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial

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