Concepedia

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The Natural History of Type B Niemann-Pick Disease: Results From a 10-Year Longitudinal Study

DOI

194

Citations

20

References

2004

Year

Melissa Wasserstein, Robert J. Desnick, Edward H. Schuchman, Sabera Hossain, Sylvan Wallenstein, Carin Lamm, Margaret M. McGovern
PEDIATRICS

Abstract

The natural history of NPD-B is characterized by hepatosplenomegaly with progressive hypersplenism, worsening atherogenic lipid profile, gradual deterioration in pulmonary function, and stable liver dysfunction.

References

YearCitations

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