Effect of ivacaftor on CFTR forms with missense mutations associated with defects in protein processing or function

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A CFTR Potentiator in Patients with Cystic Fibrosis and the <i>G551D</i> Mutation

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Rescue of CF airway epithelial cell function in vitro by a CFTR potentiator, VX-770

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Medicine, Cell Biology, Pharmacology +17

Demonstration That CFTR Is a Chloride Channel by Alteration of Its Anion Selectivity

Matthew P. Anderson, Richard J. Gregory, Simon Thompson et al. · Science · 1991 · 1.1K citations

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Correction of the F508del-CFTR protein processing defect in vitro by the investigational drug VX-809

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