Concepedia

Recombinant adeno-associated virus type 2-mediated gene delivery into the Rpe65 -/- knockout mouse eye results in limited rescue

Chooi‐May Lai, Meaghan J. T. Yu, Meliha Brankov, Nigel L. Barnett, Xiaohuai Zhou, T. Michael Redmond, Kristina Narfström, P. Elizabeth Rakoczy

Genetic Vaccines and Therapy · 2004 · 94 citations · 49 references

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49

Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield

Sergei Zolotukhin, Barry J. Byrne, Emily Grace Mason et al. · Gene Therapy · 1999 · 1.3K citations

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Gene therapy restores vision in a canine model of childhood blindness

Gregory M. Acland, Jharna Ray, Qí Zhāng et al. · Nature Genetics · 2001 · 1.2K citations

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Rpe65 is necessary for production of 11-cis-vitamin A in the retinal visual cycle

T. Michael Redmond, Shirley Yu, Eric Lee et al. · Nature Genetics · 1998 · 930 citations

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Cross-Packaging of a Single Adeno-Associated Virus (AAV) Type 2 Vector Genome into Multiple AAV Serotypes Enables Transduction with Broad Specificity

Joseph E. Rabinowitz, Fabienne Rolling, Chengwen Li et al. · Journal of Virology · 2002 · 750 citations · Full text

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Mutations in RPE65 cause autosomal recessive childhood–onset severe retinal dystrophy

Sumin Gu, Debra A. Thompson, C.R. Srikumari et al. · Nature Genetics · 1997 · 666 citations

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