Long-term correction of hyperphenylalaninemia by AAV-mediated gene transfer leads to behavioral recovery in phenylketonuria mice

Shinya Mochizuki, Hiroaki Mizukami, Tomoko Ogura, Shigeo Kure, Akiko Ichinohe, Kanako Kojima, Yoichi Matsubara, E Kobayahi, Takashi Okada, Akinori Hoshika,

Gene Therapy · 2004 · 73 citations · 27 references

Concepts

References

27