Selective Inhibition of Topoisomerase I and Various Steps of Spliceosome Assembly by Diospyrin Derivatives

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Novel Therapy, In Vivo Gene Therapy, Rna Splicing +5

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Chromatin, Natural Sciences, Rna Splicing +7

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Pathology, Pharmacotherapy, Anticancer Agents +19

Treatment of spinal muscular atrophy by sodium butyrate

Jan‐Gowth Chang, Hsiu-Mei Hsieh-Li, Yuh‐Jyh Jong et al. · Proceedings of the National Academy of Sciences · 2001 · 404 citations · Full text

Valproic acid increases the SMN2 protein level: a well-known drug as a potential therapy for spinal muscular atrophy

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