Concepedia

Restoration of Human Dystrophin Following Transplantation of Exon-Skipping-Engineered DMD Patient Stem Cells into Dystrophic Mice

Rachid Benchaouir, Mirella Meregalli, Andrea Farini, Giuseppe D’Antona, M. Belicchi, Aurélie Goyenvalle, M. Battistelli, Nereo Bresolin, Roberto Bottinelli, Luis Garcı́a,

Cell stem cell · 2007 · 223 citations · 35 references

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35

Dystrophin: The protein product of the duchenne muscular dystrophy locus

Eric P. Hoffman, Robert H. Brown, Louis M. Kunkel · Cell · 1987 · 4.7K citations

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Pax7 Is Required for the Specification of Myogenic Satellite Cells

Patrick Seale, Luc A. Sabourin, Adele Girgis-Gabardo et al. · Cell · 2000 · 2.3K citations · Full text

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Multiply attenuated lentiviral vector achieves efficient gene delivery in vivo

Romain Zufferey, Dea Nagy, Ron J. Mandel et al. · Nature Biotechnology · 1997 · 2K citations · Full text

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Dystrophin expression in the mdx mouse restored by stem cell transplantation

Emanuela Gussoni, Yuko Soneoka, Corinne D. Strickland et al. · Nature · 1999 · 1.8K citations

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Conversion of mdx myofibres from dystrophin-negative to -positive by injection of normal myoblasts

T. Partridge, Jennifer E. Morgan, Gary R. Coulton et al. · Nature · 1989 · 862 citations

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