The future of gene therapy

<i>LMO2</i> -Associated Clonal T Cell Proliferation in Two Patients after Gene Therapy for SCID-X1

S. Hacein-Bey-Abina, Christof von Kalle, Manfred Schmidt et al. · Science · 2003 · 3.6K citations

Life Sciences, Genetics, Immunology +17

Gene Therapy of Human Severe Combined Immunodeficiency (SCID)-X1 Disease

Marina Cavazzana, Salima Hacein‐Bey, Geneviève de Saint Basile et al. · Science · 2000 · 2.6K citations

Life Sciences, Genetics, Immunology +17

Correction of ADA-SCID by Stem Cell Gene Therapy Combined with Nonmyeloablative Conditioning

Alessandro Aiuti, Shimon Slavin, Memet Aker et al. · Science · 2002 · 1.1K citations

Medicine, Hematology, Immunology +15

Long-term survival and transplantation of haemopoietic stem cells for immunodeficiencies: report of the European experience 1968–99

Corinne Antoine, Susanna Müller, Andrew J. Cant et al. · The Lancet · 2003 · 574 citations

Medicine, Hematology, Immunology +16

Gene Therapy Insertional Mutagenesis Insights

Utpal P. Davé, Nancy A. Jenkins, Neal G. Copeland · Science · 2004 · 262 citations

Life Sciences, Genetics, Pediatrics +16