Characterization of Fabry Disease in 352 Pediatric Patients in the Fabry Registry

Robert J. Hopkin, John J. Bissler, Maryam Banikazemi, L. Clarke, Christine M. Eng, Dominique P. Germain, Roberta Lemay, Anna Tylki‐Szymańska, William R. Wilcox

Pediatric Research · 2008 · 304 citations · 21 references

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