Concepedia

Publication | Closed Access

Enzyme Replacement Therapy in Fabry Disease

DOI

1.3K

Citations

23

References

2001

Year

Raphael Schiffmann, Jeffrey B. Kopp, Howard A. Austin, Sharda G. Sabnis, David F. Moore, Thais Weibel, James E. Balow, Roscoe O. Brady
JAMA

Abstract

Intravenous infusions of alpha-gal A are safe and have widespread therapeutic efficacy in Fabry disease.

References

YearCitations

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