Publication | Open Access
Intravenous Infusion of an Antisense Oligonucleotide Results in Exon Skipping in Muscle Dystrophin mRNA of Duchenne Muscular Dystrophy
100
Citations
27
References
2006
Year
Exon SkippingAntisense Oligonucleotide ResultsSkeletal MuscleDuchenne Muscular DystrophyMedicineNatural SciencesDna ReplicationMolecular BiologyDegenerative DiseaseAntisense TherapyNeuromuscular PathologyCell Biology
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