Concepedia

Reported numbers of patients with rare diseases based on ten-year longitudinal national disability registries in Taiwan

Jin‐Ding Lin, Lan-Ping Lin, Wen-Jiu Hung

Research in Developmental Disabilities · 2012 · 12 citations · 17 references

DOI

Concepts

References

17

Pricing and reimbursement of orphan drugs: the need for more transparency

Steven Simoens · Orphanet Journal of Rare Diseases · 2011 · 260 citations · Full text

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Estimating the budget impact of orphan medicines in Europe: 2010 - 2020

Carina Schey, Tsveta Milanova, Adam Hutchings · Orphanet Journal of Rare Diseases · 2011 · 132 citations · Full text

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Creating a global rare disease patient registry linked to a rare diseases biorepository database: Rare Disease-HUB (RD-HUB)

Yaffa Rubinstein, Stephen C. Groft, Ronald Bartek et al. · Contemporary Clinical Trials · 2010 · 116 citations

, , +15

The common problem of rare disease in general practice

Andrew Knight, Timothy P Senior · The Medical Journal of Australia · 2006 · 116 citations

, , +15

Rare diseases: what's next?

Giuseppe Remuzzi, Silvio Garattini · The Lancet · 2008 · 40 citations

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