Nature Biotechnology · 2010 · 314 citations · 23 references
Life SciencesDevelopmental BiologyMolecular BiologyEmbryogenesisGenome EditingEmbryo ImplantationTarget Site SelectionZinc Finger NucleasesZygote FormationCleavage SpecificityZinc Finger DomainsZinc Finger MotifsZinc Finger Nuclease DesignZinc Finger Proteins
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Highly efficient endogenous human gene correction using designed zinc-finger nucleases
Fyodor D. Urnov, Jeffrey C. Miller, Ya-Li Lee et al. · Nature · 2005 · 1.6K citations